What are The Most Common Diseases that are Trying Gene Therapy?

Gene therapy has touted as a cure for many diseases such as hemophilia, cystic fibrosis, and other genetic disorders. But there are increases in the number of diseases that are being targeted or tried by gene therapy. Many of these diseases have been around for at least a decade, and have been very difficult to cure. Could gene therapy be the someday solution that everyone is looking for?

Many diseases affect a lot of people. No one is immune to any disease at any age. Gene therapy has a good standing in healing some of the most common ones.

What are The Most Common Diseases that are Trying Gene Therapy?

Gene therapy has been a hot topic in the medical community for years. It’s a new way to treat several diseases, and it’s already working for some conditions.

Gene therapy is a treatment that uses genes to treat or prevent diseases. Several gene therapies are currently researched and tested, but there are many more that has tested in the past.

The following are some of the most common diseases that have been treated through gene therapy:

1. Cancer

Cancer refers to any abnormal growth of cells that can spread around your body and damage other tissues or organs. There are many different types of cancer, but they’re all caused by changes in genes that control cell growth and DNA repair processes in your body’s cells.

Scientists have already developed several treatments based on gene therapy that can help treat certain types of cancer like melanoma (skin cancer), leukemia (blood cancer), colon cancer, breast cancer, prostate cancer, and lymphoma (lymphatic system).

2. Cystic Fibrosis

It is caused by mutations in a gene called CFTR (cystic fibrosis transmembrane conductance regulator). In healthy people, CFTR helps regulate water flow between cells in the lungs, sweat glands, pancreas, intestines, liver, testes (in males), and ovaries.


This is a virus that can cause AIDS, which stands for Acquired Immune Deficiency Syndrome. It is cause an infection with the human immunodeficiency virus (HIV), which gradually destroys your body’s ability to fight infection. Gene therapy can used to treat HIV by replacing faulty genes with healthy ones or using viruses as vectors to carry new genes into cells.

4. Hemophilia

This is a disease where you can’t make blood clots properly. People with hemophilia don’t make enough protein called clotting factor IX (or FIX). This can cause your bleeding to last longer than it should and lead to other problems, such as joint damage from repeated bleeding into joints.

5. Lupus

This is an autoimmune disease where your immune system attacks your tissues, causing inflammation in different parts of your body.

6. Sickle-cell anemia

It is a genetic disorder that affects red blood cells, making them hard and sticky like a sickle and causing them to break apart easily. The sickle shape makes them hard for red blood cells to pass through small blood vessels; this lack of oxygen can cause pain or organ damage if left untreated.

Gene therapy is a treatment that uses DNA to repair or replace genes that do not work well. It can used to treat many different types of diseases.